Mandana Arbab

Company: Boston Children’s Hospital & Harvard Medical School

Job title: Assistant Professor

Bio:

Manda Arbab is the Lodish Family Assistant Professor of Neurology at Harvard Medical School, and faculty member of the Rosamund Stone Zander Translational Neuroscience Center at Boston Children’s Hospital. She runs a research lab focused on developing develop in vivo genome editing therapeutics to cure and treat genetic neurological disorders.

Seminars:

Base Editing Rescue of Spinal Muscular Atrophy in Cells and in Mice 1:30 pm

Presenting findings from a safe, efficient, and specific AAV-based base editing approach to SMA treatment Exploring the clinical relevancy of dosing schemes used to increase therapeutic windows Follow-up studies and research areas to drive this proof-of-concept towards the clinicRead more

day: Day 1 Track B PM