GEMS: A CRISPR Epigenetics Platform to Revolutionise Genetic Medicine
Time: 1:30 pm
day: Day 1 Track A PM
Details:
- Enabling in vivo gene therapy with a hypercompact platform, dCas proteins, epigenetic modulators, and guides
- Durable gene suppression and activation after transient GEMS expression
- A de-risked platform for in vivo gene therapy: FSHD