A 101 in First-in-Human CRISPR Trials

Time: 1:00 pm
day: Pre-Conference Workshop Day


  • Setting out a framework for deciding on trial design, outcome measures, and eligibility criteria
  • Especially in a competitive field, how can we ensure enrollment is attractive for patients?
  • Considerations for preparing an onsite team to protect the quality of the treatment
  • Understanding the key regulatory requirements surrounding CRISPR personalized medicine programs and strategies to meet these
  • Developing inexpensive, fast, and robust safety and efficacy testing platforms
  • Laying out a pathway for manufacturing guides, nucleases, and vectors to the required scale for the clinical stage