Development of Systemic CRISPR-based Therapeutics

Time: 2:45 pm
day: Day Two


• Systemic non-viral delivery of CRISPR/Cas9 is a safe and effective way to perform gene editing in vivo
• Platform enables potentially curative therapies with a single IV administration
• CRISPR-mediated targeted gene insertion provides durable, high-level expression of therapeutic proteins
• Non-viral delivery to multiple tissue types opens the door to new therapeutic applications